Idebenone for the treatment of Duchenne muscular dystrophy (Protocol)
Geng J, Dong J, Jiang K, Shen L, Wu T, Ni H, Shi LL, Wang G, Wu H.
The Cochrane Library 2011.
Description of a protocol aiming at assessing efficacy of ibedenone on muscle strength, muscle function, lung function, cardiac function and quality of life for patients with DMD. The MFM is use as primary outcome to assess motor function of patients after 12 months of treatment.
Keywords: Duchenne Muscular Dystrophy, Idebenone, Treatment efficacy, Protocol, Clinical trial
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