Association Between Health-Related Quality of Life and Motor Function in Ambulant and Nonambulant Duchenne Muscular Dystrophy Patients

Gocheva V, Schmidt S, Orsini AL, Hafner P, Schaedelin S, Rueedi N, Weber P, Fischer D.
J Child Neurol. 2019. 34(14), 873-885.
This cross-sectional study showed several moderate to high correlations between different aspects of the generic and disease-specific health-related quality of life in Duchenne muscular dystrophy patients and their functional motor function.


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Mots clés : Dystrophie Musculaire de Duchenne, Pediatric Quality of Life Inventory (PedsQL), Critère de jugement clinique, Qualité de vie liée à la santé, Fonction motrice

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