Juil 17, 2020 | Articles dans les revues scientifiques, Publications
< Retour aux Publications Effects of nusinersen after one year of treatment in 123 children with SMA type 1 or 2: a French real-life observational study Audic F, de la Banda MGG, Bernoux D, Ramirez-Garcia P, Durigneux J, Barnerias C, Isapof A, Cuisset JM, Cances C,...
Juil 17, 2020 | Articles dans les revues scientifiques, Publications
< Retour aux Publications Long-term benefit of enzyme replacement therapy with alglucosidase alfa in adults with Pompe disease: prospective analysis from the French Pompe Registry Semplicini C, De Antonio M, Taouagh N, Béhin A, Bouhour F, Echaniz-Laguna A, Magot A,...
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