Motor assessment in patients with Duchenne muscular dystrophy
Diniz GP, Lasmar LM, Giannetti JG.
Arq Neuropsiquiatr. 2012. 70(6): 416-21.
This study of 20 DMD patients shows the sensitivity of the MFM with six months between two applications.
Keywords: Duchenne muscular dystrophy, MFM, Medical research concil
Articles dans les revues scientifiques
Longitudinal reliability of outcome measures in patients with Duchenne muscular dystrophy.
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Effect of Combination l-Citrulline and Metformin Treatment on Motor Function in Patients With Duchenne Muscular Dystrophy: A Randomized Clinical Trial
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Clinical trial readiness to solve barriers to drug development in FSHD (ReSolve): protocol of a large, international, multi-center prospective study.
LoRusso S, Johnson NE, McDermott MP, Eichinger K, Butterfield RJ, Carraro E, Higgs K, Lewis L, Mul K, Sacconi S, Sansone VA, Shieh P, van Engelen B, Wagner K, Wang L, Statland JM, Tawil R; ReSolve Investigators and the FSHD CTRN. BMC Neurol. 2019. 10;19(1):224. The...