Treatment with L-citrulline and metformin in Duchenne muscular dystrophy: study protocol for a single-centre, randomised, placebo-controlled trial
Hafner P, Bonati U, Rubino D, Gocheva V, Zumbrunn T, Gueven N, Fischer D.
Trials. 2016. 3;17(1):389.
Protocol of a randomised, double-blind, placebo-controlled trial aiming to demonstrate determine if treatment with L-citrulline shows a positive effect on clinical function and paraclinical biomarkers in post-polio syndrome. MFM is used as a secondary endpoint.
Keywords: L-citrulline; Post-polio syndrome; Clinical trial; Quantitative MRI
Articles in scientific journals
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