Association Between Health-Related Quality of Life and Motor Function in Ambulant and Nonambulant Duchenne Muscular Dystrophy Patients
Gocheva V, Schmidt S, Orsini AL, Hafner P, Schaedelin S, Rueedi N, Weber P, Fischer D.
J Child Neurol. 2019. 34(14):873-885.
Cross-sectional study assessing health-related quality of life (HRQOL) in ambulant and nonambulant patients with Duchenne muscular dystrophy, and explored the association between health-related quality of life and clinically assessed motor function.
Association between Pediatric Quality of Life Inventory (PedsQL) scores and overall motor abilities and the transfers and standing posture domain measured by the MFM were examined.
MFM had been found clinically meaningful in the context of a patient’s day-to-day life.
Keywords: Duchenne muscular dystrophy; Pediatric Quality of Life Inventory (PedsQL); clinical outcome measures; health-related quality of life; motor function.
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