Validity and Reliability of the 32-Item Motor Function Measure in 2- to 5-Year-Olds with Neuromuscular Disorders and 2- to 25-Year-Olds with Spinal Muscular Atrophy
Trundell D, Le Scouiller S, Gorni K, Seabrook T, Vuillerot C, SMA MFM Study Group.
Neurol Ther. 2020. 9(2):575-584.
Investigation of the validity and reliability of the MFM32 in individuals with neuromuscular disorders (NMD), including spinal muscular atrophy (SMA), aged 2-5 years, and in non-ambulant individuals with Types 2 or 3 SMA, aged 2-25 years
Results provide supportive evidence of the validity and reliability of the MFM32 in younger individuals with NMDs.
Keywords: Clinician-reported outcome; Reliability; Spinal muscular atrophy; Validity.
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