La Mesure de Fonction Motrice en maladies neuromusculaires

Groupe de recherche interdisciplinaire sur les maladies neuromusculaires.
 La minute neuromuscule 2009. 2(1).
 Presentation by the Canadian group GRIMN (Interdisciplinary Research Group on neuromuscular diseases) of the MFM as a tool for assessing motor function. (in French)

Keywords: neuromuscular diseases, scale, validation study

Articles dans les revues scientifiques

Safety and efficacy of olesoxime in patients with type 2 or non-ambulatory type 3 spinal muscular atrophy: a randomised, double-blind, placebo-controlled phase 2 trial

Bertini E, Dessaud E, Mercuri E, Muntoni F, Kirschner J, Reid C, Lusakowska A, Comi GP, Cuisset JM, Abitbol JL, Scherrer B, Ducray PS, Buchbjerg J, Vianna E, van der Pol WL, Vuillerot C, Blaettler T, Fontoura P; Olesoxime SMA Phase 2 Study Investigators Lancet Neurol....

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