Monitoring changes and predicting loss of ambulation in Duchenne muscular dystrophy with the Motor Function Measure
Vuillerot C, Girardot F, Payan C, Fermanian J, Iwaz J, de Lattre C, Bérard C.
Dev med Child Neurol 2009. 52(1): 60-65.
Changes in MFM scores of 12 DMD patients treated with corticosteroids and 54 without treatment. The results support the use of MFM in the treatment of patients with Duchenne muscular dystrophy and its use in clinical trials to evaluate patients receiving a therapy. The MFM also help to predict the loss of walk for patients with DMD.
Keywords: Duchenne Muscular Dystrophy, MFM, Corticosteroids, Loss of walk, Management of patients
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